CGTCurated CoreFDAstaleOrchard Therapeutics (Kyowa Kir…Approved
atidarsagene autotemcel (Lenmeldy, OTL-200, Libmeldy, arsa-cel)
Pre-symptomatic and early-symptomatic metachromatic leukodystrophy · ARSA (arylsulfatase A) gene
#ARSAarylsulfataseAgene#CGT#Approved#FDA-approved#BioJungboMoa-pick+5
Trials 3Status Approved