CGT

11개 · ADC 882 · Antibody 4071 · CGT 2714 · 자동 수집 갱신 권장 · 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved11 programs

데이터 갱신 주기입니다. 갱신 대기 7,666개 보기 · Curated Core는 주간 자동 동기화됩니다.

CGTAAVCurated CoreFDAstaleBioMarinApproved

valoctocogene roxaparvovec (Roctavian, BMN 270, valoctocogene roxaparvovec-rvox)

Severe hemophilia A in adults · Factor VIII (AAV5)

#FactorVIIIAAV5#CGT#Approved#FDA-approved#BioJungboMoa-pick+5
Trials 8Status Approved
CGTAAVCurated CoreFDAstaleCSL BehringApproved

etranacogene dezaparvovec (Hemgenix, AMT-061, CSL222, etranacogene dezaparvovec-drlb)

Hemophilia B (congenital Factor IX deficiency) in adults · Factor IX (AAV5 Padua)

#FactorIXAAV5Padua#CGT#Approved#FDA-approved#BioJungboMoa-pick+5
Trials 7Status Approved
CGTAAVLimited DatastaleCSL BehringPhase 3

AAV5-hFIXco-Padua (AAV5-hFIXco-Padua)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 5Status Active
CGTAAVLimited DatastaleCSL BehringPhase 3

AAV5-hFIXco-Padua (CSL222, CSL222 (AAV5-hFIXco-Padua))

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 5Status Recruiting
CGTAAVLimited DatastalePfizerPhase 3

PF-07055480 (PF-07055480, PF-07055480 (giroctocogene fitelparovec): Recombinant AAV2/6 Human Factor VIII Gene Therapy, giroctocogene fitelparovec)

Hemophilia A · Hemophilia A

#HemophiliaA#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 2Status Recruiting
CGTAAVLimited DatastaleMedical Research CouncilPhase 2

AAV2/8-HLP-FVIII-V3 (AAV2/8-HLP-FVIII-V3)

Hemophilia A · Hemophilia A

#HemophiliaA#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTAAVLimited DatastaleCSL BehringPhase 2

AAV5-hFIX (AAV5-hFIX)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTAAVLimited DatastaleCSL BehringPhase 2

AMT-061 (AAV5-hFIXco-Padua, AAV5-hFIXco-Padua (AMT-061))

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTAAVLimited DatastaleSpark Therapeutics, Inc.Phase 1

AAV8-hFIX19 (AAV8-hFIX19)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase1#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued
CGTLimited DatastaleChristian Medical College, Vell…Phase 1

Auto CD34+PBSC transduced with a lentiviral vector encoding a novel coagulation factor VIII transgene (Auto CD34+PBSC transduced with a lentiviral vector encoding a novel coagulation factor VIII transgene)

Hemophilia A · CD3

#CD3#CGT#Phase1#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTLimited DatastaleMedical College of WisconsinPhase 1

Auto CD34+PBSC, transduced with a lentiviral vector encoding the B domain deleted from of human coagulation factor VIII (Auto CD34+PBSC, transduced with a lentiviral vector encoding the B domain deleted from of human coagulation factor VIII)

Hemophilia A · CD3

#CD3#CGT#Phase1#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting