CGT

6개 · ADC 882 · Antibody 4071 · CGT 2714 · 자동 수집 갱신 권장 · 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved6 programs

데이터 갱신 주기입니다. 갱신 대기 7,666개 보기 · Curated Core는 주간 자동 동기화됩니다.

CGTAAVCurated CoreFDAstaleCSL BehringApproved

etranacogene dezaparvovec (Hemgenix, AMT-061, CSL222, etranacogene dezaparvovec-drlb)

Hemophilia B (congenital Factor IX deficiency) in adults · Factor IX (AAV5 Padua)

#FactorIXAAV5Padua#CGT#Approved#FDA-approved#BioJungboMoa-pick+5
Trials 7Status Approved
CGTAAVLimited DatastaleMeiraGTx UK II LtdPhase 2

AAV RPE65 (AAV RPE65)

Leber Congenital Amaurosis · Leber Congenital Amaurosis

#LeberCongenitalAmaurosis#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 5Status Active
CGTAAVLimited DatastaleAdrenas Therapeutics IncPhase 2

AAV BBP-631 (AAV BBP-631)

Congenital Adrenal Hyperplasia · Congenital Adrenal Hyperplasia

#CongenitalAdrenalHyperplasia#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 2Status Recruiting
CGTAAVLimited DatastaleMeiraGTx UK II LtdPreclinical

AAV OPTIRPE65 (AAV OPTIRPE65)

Leber Congenital Amaurosis (LCA); Eye Diseases · Leber Congenital Amaurosis (LCA)

#LeberCongenitalAmaurosisLCA#CGT#Preclinical#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTLimited DatastaleBeacon TherapeuticsPhase 2

rAAV2-CB-hRPE65 (rAAV2-CB-hRPE65)

Leber Congenital Amaurosis · Leber Congenital Amaurosis

#LeberCongenitalAmaurosis#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTLimited DatastaleNantes University HospitalPhase 2

rAAV2/4.hRPE65 (rAAV2/4.hRPE65)

Leber Congenital Amaurosis · Leber Congenital Amaurosis

#LeberCongenitalAmaurosis#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active