전체 프로그램

ADC 890 · Antibody 4097 · CGT 2985 · 다음 갱신 D-6 · 마지막 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved11 programs
CGTLimited DatastaleNational Heart, Lung, and Blood…Phase 2

Lentiviral G1XCGD Gene Therapy (Lentiviral G1XCGD Gene Therapy)

Granulomatous Disease, Chronic, X-linked · Granulomatous Disease, Chronic, X-linked

#GranulomatousDiseaseChronicX-lin#CGT#Phase2#cell-gene-therapy#CAR-T+5
Trials 4Status Active
CGTLimited DatastaleBeacon TherapeuticsPhase 2

rAAV2tYF-GRK1-RPGR (rAAV2tYF-GRK1-RPGR)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 4Status Recruiting
CGTAAVStandard DatabasestaleVegaVect, Inc.Phase 2

RS1 AAV Vector (RS1 AAV Vector)

Retinoschisis; X-Linked · Retinoschisis

#Retinoschisis#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 3Status Active
CGTAAVLimited DatastaleJanssen Research & Development,…Phase 2

AAV5-hRKp.RPGR (AAV5-hRKp.RPGR)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 2Status Active
CGTAAVLimited DatastaleMeiraGTx UK II LtdPhase 2

AAV5-RPGR (AAV5-RPGR)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTLimited DatastaleNational Institute of Allergy a…Phase 2

CD34+ HSCs transduced with the lentivirus vector, VSV-G pseudotyped CL20-4i-EF1α-hγc-OPT (CD34+ HSCs transduced with the lentivirus vector, VSV-G pseudotyped CL20-4i-EF1α-hγc-OPT)

X-Linked Combined Immunodeficiency Diseases · CD3

#CD3#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTAAVLimited DatastaleJanssen Research & Development,…Phase 3

Genetic: AAV5-hRKp.RPGR (Genetic: AAV5-hRKp.RPGR)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTAAVLimited DatastaleJanssen Research & Development,…Phase 3

Genetic: AAV5-hRKp.RPGR Intermediate Dose (Genetic: AAV5-hRKp.RPGR Intermediate Dose)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTLimited DatastaleGreat Ormond Street Hospital fo…Phase 2

pCCLchimGp91s lentiviral vector transduced CD34+ cells infusion (pCCLchimGp91s lentiviral vector transduced CD34+ cells infusion)

Granulomatous Disease, Chronic, X-linked, Variant · CD3

#CD3#CGT#Phase2#cell-gene-therapy#CAR-T+5
Trials 1Status Discontinued
CGTLimited DatastaleBeacon TherapeuticsPhase 2

rAAV2tYF-CB-hRS1 (rAAV2tYF-CB-hRS1)

X-linked Retinoschisis · X-linked Retinoschisis

#X-linkedRetinoschisis#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTLimited DatastaleBeacon TherapeuticsPhase 3

rAAV2tYF-GRK1-hRPGRco (rAAV2tYF-GRK1-hRPGRco)

X-Linked Retinitis Pigmentosa · X-Linked Retinitis Pigmentosa

#X-LinkedRetinitisPigmentosa#CGT#Phase3#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting