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ADC 890 · Antibody 4071 · CGT 2714 · 다음 갱신 D-4 · 마지막 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved3 programs
CGTLimited DatastaleNational Center for Research Re…Phase 1

Ornithine transcarbamylase vector (Ornithine transcarbamylase vector)

Amino Acid Metabolism, Inborn Errors · Amino Acid Metabolism, Inborn Errors

#AminoAcidMetabolismInbornErrors#CGT#Phase1#cell-gene-therapy#CAR-T+4
Trials 1Status Active
CGTLimited DatastaleEunice Kennedy Shriver National…Phase 1

recombinant adenovirus containing the ornithine transcarbamylase gene (recombinant adenovirus containing the ornithine transcarbamylase gene)

Ornithine Transcarbamylase Deficiency Disease · Ornithine Transcarbamylase Deficiency Di

#OrnithineTranscarbamylaseDeficie#CGT#Phase1#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued
CGTLimited DatastaleUltragenyx Pharmaceutical IncPhase 2

scAAV8OTC (scAAV8OTC)

Ornithine Transcarbamylase (OTC) Deficiency · Ornithine Transcarbamylase (OTC) Deficie

#OrnithineTranscarbamylaseOTCDefi#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active