CGT

4개 · ADC 882 · Antibody 4071 · CGT 2714 · 자동 수집 갱신 권장 · 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved4 programs

데이터 갱신 주기입니다. 갱신 대기 7,666개 보기 · Curated Core는 주간 자동 동기화됩니다.

CGTCurated CoreFDAstaleOrchard Therapeutics (Kyowa Kir…Approved

atidarsagene autotemcel (Lenmeldy, OTL-200, Libmeldy, arsa-cel)

Pre-symptomatic and early-symptomatic metachromatic leukodystrophy · ARSA (arylsulfatase A) gene

#ARSAarylsulfataseAgene#CGT#Approved#FDA-approved#BioJungboMoa-pick+5
Trials 3Status Approved
CGTLimited DatastaleOrchard TherapeuticsPhase 2

OTL-200 Gene Therapy (OTL-200 Gene Therapy)

Lysosomal Storage Disease; Metachromatic Leukodystrophy · Lysosomal Storage Disease

#LysosomalStorageDisease#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 3Status Active
CGTLimited DatastaleShenzhen Geno-Immune Medical In…Preclinical

Intrathecal and intravenous LV gene therapy (Intrathecal and intravenous LV gene therapy)

Metachromatic Leukodystrophy (MLD) · Metachromatic Leukodystrophy (MLD)

#MetachromaticLeukodystrophyMLD#CGT#Preclinical#cell-gene-therapy#CAR-T+2
Trials 2Status Recruiting
CGTLimited DatastaleShenzhen Geno-Immune Medical In…Preclinical

Lentiviral TYF-ARSA correction of patient's autologous HSCs (Lentiviral TYF-ARSA correction of patient's autologous HSCs)

Metachromatic Leukodystrophy (MLD) · Metachromatic Leukodystrophy (MLD)

#MetachromaticLeukodystrophyMLD#CGT#Preclinical#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting