CGTLimited DatastaleShenzhen Geno-Immune Medical In…Preclinical
Lentiviral TYF-ARSA correction of patient's autologous HSCs (Lentiviral TYF-ARSA correction of patient's autologous HSCs)
Metachromatic Leukodystrophy (MLD) · Metachromatic Leukodystrophy (MLD)
#MetachromaticLeukodystrophyMLD#CGT#Preclinical#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting