CGTAAVLimited DatastaleREGENXBIO Inc.Phase 2
AAV directed hLDLR gene therapy (AAV directed hLDLR gene therapy)
Homozygous Familial Hypercholesterolemia (HoFH) · Homozygous Familial Hypercholesterolemia
#HomozygousFamilialHypercholester#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued