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ADC 890 · Antibody 4071 · CGT 2714 · 다음 갱신 D-4 · 마지막 9월 2일

PopularRecently updatedCuratedMost trialsNeeds refreshORRLatestPhase 3FDA approved2,047 programs
CGTAAVLimited DatastaleMeiraGTx UK II LtdPreclinical

AAV OPTIRPE65 (AAV OPTIRPE65)

Leber Congenital Amaurosis (LCA); Eye Diseases · Leber Congenital Amaurosis (LCA)

#LeberCongenitalAmaurosisLCA#CGT#Preclinical#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTAAVLimited DatastaleREGENXBIO Inc.Phase 2

AAV directed hLDLR gene therapy (AAV directed hLDLR gene therapy)

Homozygous Familial Hypercholesterolemia (HoFH) · Homozygous Familial Hypercholesterolemia

#HomozygousFamilialHypercholester#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued
CGTAAVLimited DatastaleMark TuszynskiPhase 1

AAV2-BDNF Gene Therapy (AAV2-BDNF Gene Therapy)

Alzheimer's Disease; Mild Cognitive Impairment · Alzheimer's Disease

#AlzheimersDisease#CGT#Phase1#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting
CGTAAVLimited DatastaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 (AAV2-hAQP1)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTAAVLimited DatastaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 1 (AAV2-hAQP1 Concentration 1)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting
CGTAAVLimited DatastaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 2 (AAV2-hAQP1 Concentration 2)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting
CGTAAVLimited DatastaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 3 (AAV2-hAQP1 Concentration 3)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting
CGTAAVLimited DatastaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 4 (AAV2-hAQP1 Concentration 4)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Recruiting
CGTAAVLimited DatastaleeyeDNA TherapeuticsPhase 2

AAV2/5-hPDE6B (AAV2/5-hPDE6B)

Retinitis Pigmentosa · Retinitis Pigmentosa

#RetinitisPigmentosa#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued
CGTAAVLimited DatastaleCSL BehringPhase 2

AAV5-hFIX (AAV5-hFIX)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTAAVLimited DatastaleCSL BehringPhase 2

AMT-061 (AAV5-hFIXco-Padua, AAV5-hFIXco-Padua (AMT-061))

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Active
CGTAAVLimited DatastaleSpark Therapeutics, Inc.Phase 1

AAV8-hFIX19 (AAV8-hFIX19)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase1#cell-gene-therapy#CAR-T+2
Trials 1Status Discontinued
CGTAAVLimited DatastaleAspa TherapeuticsPhase 2

AAV9 BBP-812 (AAV9 BBP-812)

Canavan Disease · Canavan Disease

#CanavanDisease#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTAAVLimited DatastaleUnlimited Biotechnology LLCPhase 2

AAV9-Follistatin gene therapy (AAV9-Follistatin gene therapy)

Age-related Muscle Decline · Age-related Muscle Decline

#Age-relatedMuscleDecline#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTAAVLimited DatastaleUniQure Biopharma B.V.Phase 2

AAV9-hSyn1-miGRIK2 (AAV9-hSyn1-miGRIK2)

Mesial Temporal Lobe Epilepsy · Mesial Temporal Lobe Epilepsy

#MesialTemporalLobeEpilepsy#CGT#Phase2#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTAAVLimited DatastaleBenjamin GreenbergPhase 1

AAV9/CLN7 (AAV9/CLN7)

CLN7 · CLN7

#CLN7#CGT#Phase1#cell-gene-therapy#CAR-T+2
Trials 1Status Recruiting
CGTLimited DatastaleAkouos, Inc.Phase 2

AAVAnc80-hOTOF via Akouos Delivery Device (AAVAnc80-hOTOF via Akouos Delivery Device)

Sensorineural Hearing Loss, Bilateral · Sensorineural Hearing Loss, Bilateral

#SensorineuralHearingLossBilatera#CGT#Phase2#cell-gene-therapy#CAR-T+4
Trials 1Status Recruiting
CGTLimited DatastaleAkouos, Inc.Phase 2

AAVAnc80-hOTOF via Akouos Delivery Device and Precision Delivery Mechanism (AAVAnc80-hOTOF via Akouos Delivery Device and Precision Delivery Mechanism)

Sensorineural Hearing Loss, Bilateral · Sensorineural Hearing Loss, Bilateral

#SensorineuralHearingLossBilatera#CGT#Phase2#cell-gene-therapy#CAR-T+4
Trials 1Status Recruiting
CGTAAVLimited DatastaleWeill Medical College of Cornel…Phase 2

AAVrh.10CUCLN2 (AAVrh.10CUCLN2)

Late Infantile Neuronal Ceroid Lipofuscinosis; Batten Disease · Late Infantile Neuronal Ceroid Lipofusci

#LateInfantileNeuronalCeroidLipof#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Active
CGTAAVLimited DatastaleWeill Medical College of Cornel…Phase 1

AAVrh.10CUhCLN2 vector 2.85x10^11 genome copies (AAVrh.10CUhCLN2 vector 2.85x10^11 genome copies)

Batten Disease; Late-Infantile Neuronal Ceroid Lipofuscinosis · Batten Disease

#BattenDisease#CGT#Phase1#cell-gene-therapy#CAR-T+3
Trials 1Status Active

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