CGTAAVLimited DatastaleTippi MackenziePhase 1
Gene Transfer with an AAV9 Vector Expressing Human ß-galactosidase (Gene Transfer with an AAV9 Vector Expressing Human ß-galactosidase)
GM1 Gangliosidoses; GM1 Gangliosidosis, Type I · GM1 Gangliosidoses
#GM1Gangliosidoses#CGT#Phase1#cell-gene-therapy#CAR-T+4
Trials 1Status Recruiting