CGTAAVLimited DatastaleWeill Medical College of Cornel…Phase 2
AAVrh.10CUCLN2 (AAVrh.10CUCLN2)
Late Infantile Neuronal Ceroid Lipofuscinosis; Batten Disease · Late Infantile Neuronal Ceroid Lipofusci
#LateInfantileNeuronalCeroidLipof#CGT#Phase2#cell-gene-therapy#CAR-T+3
Trials 1Status Active