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현재 선택: 1 · 임상 갱신 필요 1

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API CSV24행 · 1개 프로그램

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항목
CGTStandard DatabasestalePhase 1
Lentiviral Gene Transfer (Lentiviral Gene Transfer)
National Human Genome Research Ins…·Adenosine Deaminase Deficiency
55 trials
Overview
Program
Lentiviral Gene Transfer
Overview
Company
National Human Genome Research Institute (NHGRI)
Overview
Modality
CGT
Overview
Target
Adenosine Deaminase Deficiency
Overview
Indication
Adenosine Deaminase Deficiency; ADA-SCID
Overview
Phase
PHASE_1
Overview
Status
ACTIVE
Overview
Content status
Standard Database
Overview
Data Confidence
Data Confidence · Medium
Overview
Development Signal
Development Signal · Watch
Overview
Approval status
Investigational
Technology
Vector
lentiviral gene transfer to downregulate orexin expression in male and female young rats t
MoA
Mechanism
targeting, which can enhance tumor-antigen
MoA
Biomarker
PD-1/PD-L1 signaling low
PK/PD
Species
Mouse, Rat
PK/PD
Animal (cat.)
Mouse, Rat, In vitro
PK/PD
Experiment
PD
Toxicology
Species
Mouse, Rat
Toxicology
Animal (cat.)
Mouse, Rat, In vitro
Toxicology
Major finding
thrombocytopenia, infections, eczema, autoimmunity, and malignant disease
Clinical
Safety signal
thrombocytopenia, infections, eczema, autoimmunity, and malignant disease
Clinical
Result source
ClinicalTrials.gov NCT01380990
Clinical
Program phase
PHASE_1
Clinical
Trial ref
NCT01380990