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프로그램 비교

타깃 · 모달리티 · 임상 근거 · 비임상 맥락으로 최대 5개 프로그램을 나란히 비교합니다. · 다음 갱신 D-6 · 마지막 9월 2일

현재 선택: 3 · 차세대 보드에서 열림

프로그램 상세에서 관심 등록 후 2개 이상 모으면 여기서 한 번에 비교할 수 있습니다.

API CSV31행 · 3개 프로그램

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항목
AntibodyCurated CoreFDAApproved
evolocumab (Repatha, AMG-145)
Amgen·PCSK9
143 trials·t½ 17 h
AntibodyCurated CoreFDAApproved
alirocumab (Praluent, REGN727, SAR236553)
Sanofi / Regeneron·PCSK9
103 trials·t½ 12 h
AntibodyCurated CoreFDAApproved
inclisiran (Leqvio, KJX839, ALN-PCS)
Novartis·PCSK9 (siRNA)
72 trials·t½ 9 h
Overview
Program
Repatha (evolocumab)Praluent (alirocumab)Leqvio (inclisiran)
Overview
Company
AmgenSanofi / RegeneronNovartis
Overview
Modality
ANTIBODYANTIBODYANTIBODY
Overview
Target
PCSK9PCSK9PCSK9 (siRNA)
Overview
Indication
Hyperlipidemia, ASCVD risk reduction, HeFH, HoFHHyperlipidemia, ASCVD, HeFHHyperlipidemia, ASCVD, HeFH (LDL-C lowering)
Overview
Phase
APPROVEDAPPROVEDAPPROVED
Overview
Status
APPROVEDAPPROVEDAPPROVED
Overview
Content status
Curated CoreCurated CoreCurated Core
Overview
Data Confidence
Data Confidence · HighData Confidence · HighData Confidence · High
Overview
Development Signal
Development Signal · EstablishedDevelopment Signal · EstablishedDevelopment Signal · Established
Overview
Approval status
FDA approvedFDA approvedFDA approved
Positioning
Key differentiator
High LDL-C lowering without statin myalgia; autoinjector penFlexible q2w dosing; post-ACS outcomes labelInfrequent dosing (q6 months maintenance)
Positioning
Known limitation
Statin non-adherence; rare anti-drug antibodiesresistance to immune checkpoint blockadeInjection-site reactions; long-term siRNA durability generally maintained.
Positioning
Development positioning
PCSK9 mAb vs inclisiran siRNA (Leqvio) dosing convenience trade-off
MoA
Mechanism
Evolocumab binds PCSK9, preventing PCSK9-mediated LDL receptor degradation on hepatocytes, increasing LDLR recycling and hepatic LDL-C clearance.Alirocumab inhibits PCSK9, increasing available LDL receptors and lowering LDL-C similarly to evolocumab.Inclisiran is a GalNAc-conjugated siRNA that catalytically degrades PCSK9 mRNA in hepatocytes, reducing PCSK9 protein and increasing LDLR density.
MoA
Biomarker
LDL-C, ApoB, non-HDL-C; Lp(a) modest reduction.LDL-C, ApoB.LDL-C, PCSK9 protein levels.
PK/PD
Half-life
17 h12 h9 h
PK/PD
Species
MouseMouse, LDL-C ↓~58%Mouse, Rat
PK/PD
Animal (cat.)
Mouse, In vitroMouseMouse, Rat, Monkey
PK/PD
Experiment
pharmacokineticpharmacokineticpharmacokinetic
Toxicology
Species
Cynomolgus monkey, Mouse, HamsterMouse, RatMouse, Rat
Toxicology
Animal (cat.)
NHP
Toxicology
Major finding
No major organ toxicity; injection-site reactionsInjection-site reactions, flu-like symptoms.Injection-site reactions, arthralgia, urinary tract infection.
Toxicology
CRS
N/AN/AN/A
Clinical
Safety signal
No major organ toxicity; injection-site reactionsInjection-site reactions, flu-like symptoms.Injection-site reactions, arthralgia, urinary tract infection.
Clinical
Selected reported efficacy
67%
Clinical
Result source
ClinicalTrials.gov NCT05144529
Clinical
Program phase
APPROVEDAPPROVEDAPPROVED
Clinical
Trial activity
No active/completed countsNo active/completed countsNo active/completed counts
Clinical
Trial ref
NCT05144529
Preclinical
Animal (cat.)
Mouse, In vitroMouseMouse
Repatha (evolocumab) vs Praluent (alirocumab) vs Leqvio (inclisiran) 비교 | 바이오정보모아