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타깃 · 모달리티 · 임상 근거 · 비임상 맥락으로 최대 5개 프로그램을 나란히 비교합니다. · 다음 갱신 D-4 · 마지막 9월 2일

현재 선택: 1 · 임상 갱신 필요 1

프로그램 상세에서 관심 등록 후 2개 이상 모으면 여기서 한 번에 비교할 수 있습니다.

API CSV14행 · 1개 프로그램

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항목
CGTStandard DatabasestalePhase 3
rAAV2tYF-GRK1-hRPGRco (rAAV2tYF-GRK1-hRPGRco)
Beacon Therapeutics·X-Linked Retinitis Pigmentosa
1 trials
Overview
Program
rAAV2tYF-GRK1-hRPGRco
Overview
Company
Beacon Therapeutics
Overview
Modality
CGT
Overview
Target
X-Linked Retinitis Pigmentosa
Overview
Indication
X-Linked Retinitis Pigmentosa
Overview
Phase
PHASE_3
Overview
Status
RECRUITING
Overview
Content status
Standard Database
Overview
Data Confidence
Data Confidence · Medium
Overview
Development Signal
Development Signal · Emerging
Overview
Approval status
Investigational
Toxicology
Major finding
Toxicity and Efficacy Evaluation of an Adeno-Associated Virus Vector Expressing Codon-Optimized RPGR Delivered by Subretinal Injection in a Canine Model of X-linked Retinitis Pigmentosa.. Applied Genetic Technologies Corporation (AGTC) is developing a recombinant adeno-associated virus (rAAV) vector AGTC-501, also designated rAAV2tYF-GRK1- hRPGRco , to treat X-linked retinitis pigmentosa (XLRP) in…
Clinical
Safety signal
Toxicity and Efficacy Evaluation of an Adeno-Associated Virus Vector Expressing Codon-Optimized RPGR Delivered by Subretinal Injection in a Canine Model of X-linked Retinitis Pigmentosa.. Applied Genetic Technologies Corporation (AGTC) is developing a recombinant adeno-associated virus (rAAV) vector AGTC-501, also designated rAAV2tYF-GRK1- hRPGRco , to treat X-linked retinitis pigmentosa (XLRP) in…
Clinical
Program phase
PHASE_3