AB-1009 (GAA Gene) 비교 | 바이오정보모아

프로그램 상세에서 관심 등록 후 2개 이상 모으면 여기서 한 번에 비교할 수 있습니다.

프로그램 선택

Overview PK/PD Toxicology Clinical

표가 넓으면 좌우로 스크롤하세요. 핵심 비교 모드에서는 중요 항목만 표시됩니다.

항목	CGTStandard DatabasestalePhase 2 GAA Gene (AB-1009, AB-1009 (GAA Gene)) AskBio Inc·Pompe Disease (Late-onset) 19 trials·t½ 3.1 h

Overview Program	AB-1009 (GAA Gene)
Overview Company	AskBio Inc
Overview Modality	CGT
Overview Target	Pompe Disease (Late-onset)
Overview Indication	Pompe Disease (Late-onset); Pompe Disease Late-Onset
Overview Phase	PHASE_2
Overview Status	RECRUITING
Overview Content status	Standard Database
Overview Data Confidence	Data Confidence · Medium
Overview Development Signal	Development Signal · Emerging
Overview Approval status	Investigational

PK/PD Half-life	3.1 h

Toxicology Major finding	thrombocytopenia, thrombotic microangiopathy, and hemophagocytic lymphohistiocytosis), and Pompe

Clinical Safety signal	thrombocytopenia, thrombotic microangiopathy, and hemophagocytic lymphohistiocytosis), and Pompe
Clinical Program phase	PHASE_2

프로그램 상세에서 관심 등록 후 2개 이상 모으면 여기서 한 번에 비교할 수 있습니다.

프로그램 선택

Overview PK/PD Toxicology Clinical

표가 넓으면 좌우로 스크롤하세요. 핵심 비교 모드에서는 중요 항목만 표시됩니다.

항목	CGTStandard DatabasestalePhase 2 GAA Gene (AB-1009, AB-1009 (GAA Gene)) AskBio Inc·Pompe Disease (Late-onset) 19 trials·t½ 3.1 h

Overview Program	AB-1009 (GAA Gene)
Overview Company	AskBio Inc
Overview Modality	CGT
Overview Target	Pompe Disease (Late-onset)
Overview Indication	Pompe Disease (Late-onset); Pompe Disease Late-Onset
Overview Phase	PHASE_2
Overview Status	RECRUITING
Overview Content status	Standard Database
Overview Data Confidence	Data Confidence · Medium
Overview Development Signal	Development Signal · Emerging
Overview Approval status	Investigational

PK/PD Half-life	3.1 h

Toxicology Major finding	thrombocytopenia, thrombotic microangiopathy, and hemophagocytic lymphohistiocytosis), and Pompe

Clinical Safety signal	thrombocytopenia, thrombotic microangiopathy, and hemophagocytic lymphohistiocytosis), and Pompe
Clinical Program phase	PHASE_2